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Kabuki Syndrome Foundation Announces New Therapy Development Fund

Therapy Development Fund. Advancing Treatments Toward Trials. Kabuki Syndrome Foundation.

Strategic investments targeting therapies already in development will average between $150,000 – $250,000.

Why We Need The Therapy Development Fund

Rare disease research faces a significant hurdle in bridging the gap between basic science and taking potential treatments to clinical trials, and ultimately patients. Promising discoveries in the lab often fail to move forward due to a lack of funding. The Therapy Development Fund can bridge this gap, by funding research that can meaningfully advance potential treatments from proof-of-concept to clinical trials. This can include, but is not limited to, studies to better understand the safety and efficacy of a potential treatment. 

“Our community plays a crucial role in rare disease drug development, and the Kabuki Syndrome Foundation is thrilled to offer this new grant program to advance potential treatments toward clinical trials with the hope of drastically improving the lives of patients and their families,” said Janet Lee, Executive Director of the Kabuki Syndrome Foundation. 

Funding Treatments for Kabuki Syndrome

The Therapy Development Fund is our latest initiative in LEAP, the roadmap to Kabuki syndrome treatments. LEAP was designed to accelerate and enable treatment development for people with Kabuki syndrome around the world. Over $2,000,000 has been secured to support LEAP so far. 

We are the only organization funding the discovery and development of therapeutics that will improve the lives of people with Kabuki syndrome, and we need your help. It takes millions of dollars to get just one potential treatment from the lab to people living with Kabuki syndrome. Please visit our donate page – share it with your friends and family – and take advantage of the many ways you can donate.

Therapy Development Fund Details

The Therapy Development Fund is open to academic and industry investigators. For more information or to apply for funding, please see our Grant Opportunities